Dual Purpose Vectors for Rare Neurological Diseases: Molecular Therapy

Curative gene therapies for rare diseases

Gene Therapy Preserves Retinal Structure and Function in a Mouse Model of NMNAT1-Associated Retinal Degeneration: Molecular Therapy - Methods & Clinical Development

Coave Therapeutics – Coave Therapeutics is a clinical stage biotechnology company focused on developing life changing gene therapies in rare ocular and CNS (Central Nervous System) diseases.

Pronounced Therapeutic Benefit of a Single Bidirectional AAV Vector Administered Systemically in Sandhoff Mice: Molecular Therapy

Frontiers Vectored Immunotherapeutics for Infectious Diseases: Can rAAVs Be The Game Changers for Fighting Transmissible Pathogens?

Frontiers Current and Future Prospects for Gene Therapy for Rare Genetic Diseases Affecting the Brain and Spinal Cord

Frontiers AAV-mediated gene therapy: Advancing cardiovascular disease treatment

Biomolecules, Free Full-Text

Utilization and Potential of RNA-Based Therapies in Cardiovascular Disease - ScienceDirect

Full article: Gene therapy for neurological disorders: challenges and recent advancements